المؤلفون: Cong, Wang, Mingli, Ding, Shuangyu, Wei, Xian, Li, Zhenning, He

المصدر: 2017 First International Conference on Electronics Instrumentation & Information Systems (EIIS) Electronics Instrumentation & Information Systems (EIIS), 2017 First International Conference on. :1-5 Jun, 2017

Relation: 2017 First International Conference on Electronics Instrumentation & Information Systems (EIIS)

المؤلفون: Mingli, Ding, Wei, Ye, Cong, Wang, Xi, Yan, Zhenning, He, Jintao, Yu

المصدر: 2017 First International Conference on Electronics Instrumentation & Information Systems (EIIS) Electronics Instrumentation & Information Systems (EIIS), 2017 First International Conference on. :1-5 Jun, 2017

Relation: 2017 First International Conference on Electronics Instrumentation & Information Systems (EIIS)

المؤلفون: Lili Wang, Claude C. Warzecha, Alexander Kistner, Jessica A. Chichester, Peter Bell, Elizabeth L. Buza, Zhenning He, M. Betina Pampena, Julien Couthouis, Sunjay Sethi, Kathleen McKeever, Michael R. Betts, Emil Kakkis, James M. Wilson, Samuel Wadsworth, Barbara A. Sullivan

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 24, Iss , Pp 292-305 (2022)

مصطلحات موضوعية: adeno-associated virus, AAV8, ornithine transcarbamylase deficiency, non-human primates, sex, immunosuppression, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050122000080; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/0bb545c351f24bafb56d6307da45c4b4

المؤلفون: Lili Wang, Ilayaraja Muthuramu, Suryanarayan Somanathan, Hong Zhang, Peter Bell, Zhenning He, Hongwei Yu, Yanqing Zhu, Anna P. Tretiakova, James M. Wilson

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 22, Iss , Pp 1-10 (2021)

مصطلحات موضوعية: familial hypercholesterolemia, adeno-associated virus, gene therapy, LDLR, LDL, codon optimization, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050121000838; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/4767aca2c6484388aa3a62ba41dc1ac8

المؤلفون: Hongwei Yu, Zhenning He, Yanqing Zhu, Hong Zhang, Ilayaraja Muthuramu, Lili Wang, James M. Wilson, Suryanarayan Somanathan, Anna Tretiakova, Peter Bell

المصدر: Molecular Therapy. Methods & Clinical Development
Molecular Therapy: Methods & Clinical Development, Vol 22, Iss, Pp 1-10 (2021)

مصطلحات موضوعية: 0301 basic medicine, Transgene, Genetic enhancement, HoFH, adeno-associated virus, Familial hypercholesterolemia, QH426-470, Biology, medicine.disease_cause, LDL, codon optimization, 03 medical and health sciences, 0302 clinical medicine, Genetics, medicine, Vector (molecular biology), liver-directed, Molecular Biology, Adeno-associated virus, Gene, QH573-671, familial hypercholesterolemia, medicine.disease, gene therapy, LDLR, 030104 developmental biology, 030220 oncology & carcinogenesis, LDL receptor, Cancer research, Molecular Medicine, Original Article, lipids (amino acids, peptides, and proteins), AAV8, Cytology, Lipoprotein

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::52b537347f6e30d4bda394563ce89d49
https://doi.org/10.1016/j.omtm.2021.04.017

المؤلفون: Jenny A. Greig, Camilo Breton, Kelly M. Martins, Yanqing Zhu, Zhenning He, John White, Peter Bell, Lili Wang, James M. Wilson

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::58544596b0e55c88705510ccddbb3838
https://doi.org/10.1101/2022.03.24.485675

المؤلفون: Camilo Breton, James M. Wilson, Derek Jantz, Yanqing Zhu, Peter Bell, Claude C. Warzecha, John H. White, Mingyao Li, Hanying Yan, Lili Wang, Elizabeth L. Buza, Zhenning He

المصدر: Mol Ther

مصطلحات موضوعية: Primates, Genetic enhancement, Genetic Vectors, Gene Expression, Pharmacology, 03 medical and health sciences, chemistry.chemical_compound, Mice, 0302 clinical medicine, Genome editing, Drug Discovery, Genetics, Medicine, Animals, Molecular Biology, 030304 developmental biology, Gene Editing, Mice, Knockout, 0303 health sciences, Gene knockdown, business.industry, PCSK9, Gene Transfer Techniques, Genetic Therapy, Dependovirus, Proprotein convertase, Lipoproteins, LDL, Disease Models, Animal, chemistry, Liver, 030220 oncology & carcinogenesis, Low-density lipoprotein, Molecular Medicine, Kexin, Original Article, CRISPR-Cas Systems, Proprotein Convertase 9, business, Lipoprotein

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::32d97b4142a9dd36fa1404ce66ff5d69
https://pubmed.ncbi.nlm.nih.gov/33609733

المؤلفون: James M. Wilson, Mark L. Batshaw, John H. White, Peter Bell, Chenyu Xu, Yang Yang, Yan Che, Hiroki Morizono, Jia Zhang, Deirdre McMenamin, Mingyao Li, Caitlin Latshaw, Camilo Breton, Alexei Saveliev, Lili Wang, Hongwei Yu, Zhenning He

المصدر: Science Advances

مصطلحات موضوعية: Male, Time Factors, DNA Repair, Urea cycle disorder, viruses, Genetic enhancement, Genetic Vectors, Ornithine transcarbamylase, Biology, medicine.disease_cause, Mice, 03 medical and health sciences, 0302 clinical medicine, INDEL Mutation, medicine, Animals, Health and Medicine, Ornithine Carbamoyltransferase, Research Articles, Ornithine transcarbamylase deficiency, 030304 developmental biology, 0303 health sciences, Mutation, Multidisciplinary, SciAdv r-articles, Gene targeting, Human Genetics, Hyperammonemia, Genetic Therapy, Dependovirus, medicine.disease, Ornithine Carbamoyltransferase Deficiency Disease, 3. Good health, Disease Models, Animal, Liver, Genetic Loci, 030220 oncology & carcinogenesis, Gene Targeting, Cancer research, Dietary Proteins, CRISPR-Cas Systems, Research Article, Minigene

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::0fa1eb0f5acd3a58718c99944a4eebe9
https://doi.org/10.1126/sciadv.aax5701

المؤلفون: John H. White, Zhenning He, Yan Che, Alexei Saveliev, Yang Yang, James M. Wilson, Caitlin Latshaw, Camilo Breton, Lili Wang, Deirdre McMenamin, Jia Zhang, Mingyao Li

المصدر: Blood. 133(26)

مصطلحات موضوعية: 0301 basic medicine, Genetic enhancement, Immunology, Genetic Vectors, 030204 cardiovascular system & hematology, medicine.disease_cause, Biochemistry, Hemophilia B, Factor IX, 03 medical and health sciences, Mice, 0302 clinical medicine, Medicine, CRISPR, Animals, Humans, Vector (molecular biology), Mice, Knockout, Mutation, Hemostasis, business.industry, Cas9, Gene targeting, Cell Biology, Hematology, Genetic Therapy, Dependovirus, 030104 developmental biology, Animals, Newborn, Knockout mouse, Gene Targeting, CRISPR-Cas Systems, business, medicine.drug

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::ded1f8eef171bfd0af0328f660b0cac9
https://pubmed.ncbi.nlm.nih.gov/31248872

المؤلفون: Mark L. Batshaw, Deirdre McMenamin, John H. White, Hongwei Yu, Zhenning He, James M. Wilson, Peter Bell, Chenyu Xu, Hiroki Morizono, Lili Wang, Yang Yang, Kiran Musunuru

المصدر: Nature biotechnology

مصطلحات موضوعية: 0301 basic medicine, medicine.medical_specialty, Urea cycle disorder, Genetic enhancement, Genetic Vectors, Biomedical Engineering, Ornithine transcarbamylase, Bioengineering, Biology, medicine.disease_cause, Applied Microbiology and Biotechnology, Article, Virus, Mice, 03 medical and health sciences, Liver disease, Internal medicine, medicine, Animals, Humans, Gene, Ornithine Carbamoyltransferase, Mutation, Gene Transfer Techniques, Hyperammonemia, Dependovirus, medicine.disease, Molecular biology, Ornithine Carbamoyltransferase Deficiency Disease, 3. Good health, Disease Models, Animal, 030104 developmental biology, Endocrinology, Viruses, Molecular Medicine, RNA Editing, CRISPR-Cas Systems, Biotechnology

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::7b0784d3f6efcc46e1cfc8aefd9044a0
https://doi.org/10.1038/nbt.3469