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المؤلفون: Yoshitsugu Aoki, A Arzumanov, Kamel Mamchaoui, Tone Yuichiro, Rika Maruyama, Graham McClorey, Shin'ichi Takeda, Toshifumi Yokota, Yasumasa Hashimoto, Maria K. Tsoumpra, Michihiro Imamura, Vincent Mouly, Michael J. Gait, Matthew J.A. Wood, Reiko Terada
المساهمون: Gestionnaire, HAL Sorbonne Université 5, Department of Neuromuscular Research, National Institute of Neuroscience, National Center of Neurology and Psychiatry, Centre de recherche en Myologie – U974 SU-INSERM, Institut National de la Santé et de la Recherche Médicale (INSERM)-Sorbonne Université (SU), University of Alberta, University of Oxford, UMRS974, Université Pierre et Marie Curie - Paris 6 (UPMC), University of Oxford [Oxford], Institut de Myologie, Centre National de la Recherche Scientifique (CNRS)-Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Commissariat à l'énergie atomique et aux énergies alternatives (CEA)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Association française contre les myopathies (AFM-Téléthon)-Sorbonne Université (SU), Centre de Recherche en Myologie
المصدر: Nucleic Acid Therapeutics
Nucleic Acid Therapeutics, 2021, 31 (2), pp.172-181. ⟨10.1089/nat.2020.0907⟩
Nucleic Acid Therapeutics, Mary Ann Liebert, Inc. publishers, 2021, 31 (2), pp.172-181. ⟨10.1089/nat.2020.0907⟩مصطلحات موضوعية: 0301 basic medicine, canine X-linked muscular dystrophy in Japan (CXMD J ), Duchenne muscular dystrophy, Biochemistry, Morpholinos, Dystrophin, Myoblasts, Mice, 0302 clinical medicine, Drug Discovery, Muscular dystrophy, Telomerase, ComputingMilieux_MISCELLANEOUS, biology, Chemistry, Myogenesis, phosphorodiamidate morpholino oligomer, Exons, Original Papers, 3. Good health, Cell biology, 030220 oncology & carcinogenesis, Molecular Medicine, [SDV.MHEP.AHA] Life Sciences [q-bio]/Human health and pathology/Tissues and Organs [q-bio.TO], splice-switching oligonucleotides, Nonsense mutation, [SDV.BC]Life Sciences [q-bio]/Cellular Biology, Cell Line, 03 medical and health sciences, Dogs, Genetics, medicine, [SDV.MHEP.AHA]Life Sciences [q-bio]/Human health and pathology/Tissues and Organs [q-bio.TO], Animals, Humans, Telomerase reverse transcriptase, Molecular Biology, Cyclin-Dependent Kinase 4, Genetic Therapy, immortalized dystrophic canine myoblast, Oligonucleotides, Antisense, canine X-linked muscular dystrophy in Japan (CXMDJ), medicine.disease, Exon skipping, Muscular Dystrophy, Duchenne, 030104 developmental biology, biology.protein, Cell-penetrating peptide, RNA Splice Sites, Peptides, cell-penetrating peptide
وصف الملف: application/pdf
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::37e6bb92dfaba5985c0590e408a2e368
https://hal.sorbonne-universite.fr/hal-03276095 -
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