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1دورية أكاديمية
المؤلفون: Sheikh, Omar, Yokota, ToshifumiAff1, IDs0020402103184z_cor2
المصدر: Archives of Toxicology. 96(1):1-9
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2دورية أكاديميةInjection site reactions after long-term subcutaneous delivery of drisapersen: a retrospective study
المؤلفون: Hilhorst, NielsAff1, Spanoudi-Kitrimi, IfigeniaAff1, Goemans, NathalieAff2, Morren, Marie-AnneAff1
المصدر: European Journal of Pediatrics. 178(2):253-258
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3دورية أكاديمية
المصدر: Orphanet Journal of Rare Diseases, Vol 13, Iss 1, Pp 1-13 (2018)
مصطلحات موضوعية: Eteplirsen, Drisapersen, Randomized controlled trial, Pooled estimates, 6-min walk test, Prospectively planned meta-analysis, Medicine
وصف الملف: electronic resource
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4دورية أكاديمية
المؤلفون: Shimizu-Motohashi, YukoAff1, Murakami, TerumiAff2, Kimura, EnAff3, Komaki, Hirofumi, Watanabe, NorioAff4
المصدر: Orphanet Journal of Rare Diseases. 13(1)
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المؤلفون: Sudhir Agarwal, Rakesh N. Veedu, Bao T. Le
المصدر: RSC Advances. 11:14029-14035
مصطلحات موضوعية: chemistry.chemical_classification, 0303 health sciences, Morpholino, Chemistry, General Chemical Engineering, RNA, General Chemistry, Computational biology, Exon skipping, 03 medical and health sciences, Exon, chemistry.chemical_compound, 0302 clinical medicine, 030220 oncology & carcinogenesis, splice, Nucleotide, DNA, Drisapersen, 030304 developmental biology
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::eed747a78bcc6c90aaeb49f99626b468
https://doi.org/10.1039/d1ra00878a -
6دورية أكاديمية
لا يتم عرض هذه النتيجة على الضيوف.
تسجيل الدخول للوصول الكامل. -
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المؤلفون: Nicole A. Datson, Cathaline den Besten, Judith C.T. van Deutekom, Sieto Bosgra, Sjef J. de Kimpe, Jessica A. Sipkens
المصدر: Nucleic Acid Therapeutics. 29:305-322
مصطلحات موضوعية: 0301 basic medicine, Oligonucleotide, business.industry, Duchenne muscular dystrophy, Computational biology, medicine.disease, Biochemistry, Exon skipping, Clinical trial, 03 medical and health sciences, 030104 developmental biology, 0302 clinical medicine, Pharmacokinetics, 030220 oncology & carcinogenesis, Pharmacodynamics, Drug Discovery, Genetics, medicine, Molecular Medicine, Distribution (pharmacology), business, Molecular Biology, Drisapersen
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::75f7c6184e4d7580eb6c29c0db62263d
https://doi.org/10.1089/nat.2019.0805 -
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المصدر: Frontiers in Pharmacology
Frontiers in Pharmacology, Vol 12 (2021)مصطلحات موضوعية: EXPRESSION, medicine.medical_specialty, utrophin upregulation, Duchenne muscular dystrophy, Genetic enhancement, randomized controlled clinical trials, Medizin, myostatin inhibition, Cardiomyopathy, RM1-950, PHASE-2 TRIAL, MYOSTATIN, dystrophin, OPEN-LABEL EXTENSION, DRISAPERSEN, SYSTEMIC DELIVERY, Medicine, Pharmacology (medical), Pharmacology & Pharmacy, GLUCOCORTICOIDS, ANTISENSE OLIGONUCLEOTIDE, Intensive care medicine, duchenne muscular dystrophy, Pharmacology, clinical trials, Science & Technology, RESPIRATORY-FUNCTION, biology, business.industry, medicine.disease, Exon skipping, Clinical trial, Perspective, Antisense oligonucleotides, biology.protein, Life expectancy, IDEBENONE, Therapeutics. Pharmacology, antisense oligonucleotides, business, Dystrophin, Life Sciences & Biomedicine, exon skipping
وصف الملف: Electronic-eCollection
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::317df4bb811a70872a7e3606c985db0b
https://doi.org/10.3389/fphar.2021.735912 -
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المؤلفون: Barry J. Byrne, Olga Mitelman, Sourav Santra, Jerry R. Mendell, Ashish Dugar, Anne M. Connolly, Hoda Z. Abdel-Hamid, Nathalie Goemans, Eugenio Mercuri, Peter Heydemann, Kathryn R. Wagner, Craig M. McDonald, Crystal Proud, Perry B. Shieh, James Signorovitch
المصدر: Journal of neuromuscular diseases. 9(1)
مصطلحات موضوعية: Duchenne muscular dystrophy, Male, Vital capacity, medicine.medical_specialty, Time Factors, 6-minutewalk test, Adolescent, Vital Capacity, Clinical Neurology, Walk Test, Eteplirsen, dystrophin, Pulmonary function testing, Morpholinos, DUCHENNE MUSCULAR-DYSTROPHY, 6-MINUTE WALK TEST, FEV1/FVC ratio, DRISAPERSEN, forced vital capacity, loss of ambulation, Internal medicine, END-POINTS, Outcome Assessment, Health Care, Medicine, Humans, eteplirsen, Prospective Studies, Registries, Mobility Limitation, Child, Retrospective Studies, Science & Technology, business.industry, Proportional hazards model, DISEASE PROGRESSION, Neurosciences, Repeated measures design, NATURAL-HISTORY, Muscular Dystrophy, Duchenne, Neurology, Ambulatory, Disease Progression, TRIAL, Neurosciences & Neurology, Neurology (clinical), business, Life Sciences & Biomedicine, Natural history study
وصف الملف: Print
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::00a25355a896eeef4db17d9cfa0c69a6
https://pubmed.ncbi.nlm.nih.gov/34420980 -
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المؤلفون: Omar Sheikh, Toshifumi Yokota
المصدر: Archives of toxicology. 96(1)
مصطلحات موضوعية: Male, Morpholino, Health, Toxicology and Mutagenesis, Duchenne muscular dystrophy, Toxicology, Bioinformatics, Eteplirsen, Morpholinos, medicine, Humans, Adverse effect, Child, Drisapersen, biology, business.industry, Infant, Newborn, General Medicine, Exons, Oligonucleotides, Antisense, medicine.disease, Clinical trial, Muscular Dystrophy, Duchenne, Tolerability, biology.protein, business, Dystrophin