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1دورية أكاديمية
المؤلفون: Marti Cabanes-Creus, Renina Gale Navarro, Erhua Zhu, Grober Baltazar, Sophia H.Y. Liao, Matthieu Drouyer, Anais K. Amaya, Suzanne Scott, Loan Hanh Nguyen, Adrian Westhaus, Matthias Hebben, Laurence O.W. Wilson, Adrian J. Thrasher, Ian E. Alexander, Leszek Lisowski
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 24, Iss , Pp 88-101 (2022)
مصطلحات موضوعية: AAV, adeno-associated vectors, bioengineering, bioengineered vectors, gene therapy, liver-tropic, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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المؤلفون: Sophia H.Y. Liao, Suzanne Scott, Erhua Zhu, Loan Hanh Nguyen, Adrian Westhaus, Adrian J. Thrasher, Grober Baltazar, Renina Gale Navarro, Anais K. Amaya, Marti Cabanes-Creus, Leszek Lisowski, Matthieu Drouyer, Laurence O. W. Wilson, Ian E. Alexander, Matthias Hebben
المصدر: Molecular Therapy. Methods & Clinical Development
Molecular Therapy: Methods & Clinical Development, Vol 24, Iss, Pp 88-101 (2022)مصطلحات موضوعية: bioengineered vectors, viruses, Transgene, xenograft model, Computational biology, QH426-470, Gene delivery, Vectors in gene therapy, Biology, recombinant vectors, Transduction (genetics), Genetics, Molecular Biology, Tropism, bioengineering, QH573-671, Mechanism (biology), AAV, adeno-associated vectors, Directed evolution, gene therapy, preclinical liver model, Capsid, Molecular Medicine, Original Article, Cytology, liver-tropic
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3دورية أكاديمية
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4دورية أكاديمية
المؤلفون: Cabanes-Creus M; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia., Navarro RG; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia., Zhu E; Gene Therapy Research Unit, Children's Medical Research Institute & The Children's Hospital at Westmead, The University of Sydney, Westmead, NSW 2145, Australia., Baltazar G; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia., Liao SHY; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia., Drouyer M; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia., Amaya AK; Gene Therapy Research Unit, Children's Medical Research Institute & The Children's Hospital at Westmead, The University of Sydney, Westmead, NSW 2145, Australia., Scott S; Gene Therapy Research Unit, Children's Medical Research Institute & The Children's Hospital at Westmead, The University of Sydney, Westmead, NSW 2145, Australia.; Commonwealth Scientific and Industrial Research Organisation (CSIRO), North Ryde, NSW 2113, Australia., Nguyen LH; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia., Westhaus A; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia.; Great Ormond Institute of Child Health, University College London, WC1N 1EH London, UK., Hebben M; LogicBio Therapeutics, 65 Hayden avenue, Lexington, 02421 MA, USA., Wilson LOW; Commonwealth Scientific and Industrial Research Organisation (CSIRO), North Ryde, NSW 2113, Australia., Thrasher AJ; Great Ormond Institute of Child Health, University College London, WC1N 1EH London, UK., Alexander IE; Gene Therapy Research Unit, Children's Medical Research Institute & The Children's Hospital at Westmead, The University of Sydney, Westmead, NSW 2145, Australia.; Discipline of Child and Adolescent Health, The University of Sydney, Sydney Medical School, Faculty of Medicine and Health, Westmead, NSW 2145, Australia., Lisowski L; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia.; Vector and Genome Engineering Facility, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia.; Military Institute of Medicine, Laboratory of Molecular Oncology and Innovative Therapies, 04-141 Warsaw, Poland.
المصدر: Molecular therapy. Methods & clinical development [Mol Ther Methods Clin Dev] 2021 Nov 25; Vol. 24, pp. 88-101. Date of Electronic Publication: 2021 Nov 25 (Print Publication: 2022).
نوع المنشور: Journal Article
بيانات الدورية: Publisher: Cell Press Country of Publication: United States NLM ID: 101624857 Publication Model: eCollection Cited Medium: Print ISSN: 2329-0501 (Print) Linking ISSN: 23290501 NLM ISO Abbreviation: Mol Ther Methods Clin Dev Subsets: PubMed not MEDLINE