المؤلفون: Tordo, Julie, O'Leary, Claire, Antunes, André S.L.M., Palomar, Nuria, Aldrin-Kirk, Patrick, Basche, Mark, Bennett, Antonette, D'Souza, Zelpha, Gleitz, Hélène, Godwin, Annie, Holley, Rebecca J., Parker, Helen, Liao, Ai Yin, Rouse, Paul, Youshani, Amir Saam, Dridi, Larbi, Martins, Carla, Levade, Thierry, Stacey, Kevin B., Davis, Daniel M., Dyer, Adam, Clément, Nathalie, Björklund, Tomas, Ali, Robin R., Agbandje-McKenna, Mavis, Rahim, Ahad A., Pshezhetsky, Alexey, Waddington, Simon N., Linden, R. Michael, Bigger, Brian W., Henckaerts, Els

المصدر: Brain MultiPark: Multidisciplinary research focused on Parkinson´s disease. 141(7):2014-2031

مصطلحات موضوعية: adeno-associated virus, capsid engineering, lysosomal transmembrane enzyme, mucopolysaccharidosis, neurotropism, Medicin och hälsovetenskap, Medicinska och farmaceutiska grundvetenskaper, Cell- och molekylärbiologi, Medical and Health Sciences, Basic Medicine, Cell and Molecular Biology

URL الوصول: https://lup.lub.lu.se/record/2bac8ee7-ab26-4a25-8f23-533ebd554c17
http://dx.doi.org/10.1093/brain/awy126

المؤلفون: R. Michael Linden, Els Henckaerts, Rebecca J. Holley, Antonette Bennett, Patrick Aldrin-Kirk, Robin R. Ali, Amir Saam Youshani, Carla Martins, Alexey V. Pshezhetsky, Mavis Agbandje-McKenna, Brian W. Bigger, André S L M Antunes, Thierry Levade, Julie Tordo, Helen Parker, Paul Rouse, Zelpha D'Souza, Larbi Dridi, Kevin B. Stacey, Ahad A. Rahim, Annie Godwin, Nathalie Clement, Claire O'Leary, Daniel M. Davis, Ai Yin Liao, Simon N. Waddington, Nuria Palomar, Mark Basche, Hélène F.E. Gleitz, Adam Dyer, Tomas Björklund

المصدر: Brain
Tordo, J, O'Leary, C, Antunes, A S L M, Palomar, N, Aldrin-Kirk, P, Basche, M, Bennett, A, D'Souza, Z, Gleitz, H, Godwin, A, Holley, R J, Parker, H, Liao, A Y, Rouse, P, Youshani, A S, Dridi, L, Martins, C, Levade, T, Stacey, K B, Davis, D M, Dyer, A, Clément, N, Björklund, T, Ali, R R, Agbandje-McKenna, M, Rahim, A A, Pshezhetsky, A, Waddington, S N, Linden, R M, Bigger, B W & Henckaerts, E 2018, ' A novel adeno-associated virus capsid with enhanced neurotropism corrects a lysosomal transmembrane enzyme deficiency ', Brain, vol. 141, no. 7, pp. 2014-2031 . https://doi.org/10.1093/brain/awy126
Tordo, J, O'Leary, C, Antunes, A S L M, Palomar, N, Aldrin-Kirk, P, Basche, M, Bennett, A, D'Souza, Z, Gleitz, H, Godwin, A, Holley, R, Parker, H, Liao, A, Rouse, P, Youshani, A, Dridi, L, Martins, C, Levade, T, Stacey, K, Davis, D M, Dyer, A, Clement, N, Bjorklund, T, Ali, R R, Agbandje-McKenna, M, Rahim, A, Pshezhetsky, A V, Waddington, S N, Linden, R M, Bigger, B & Henckaerts, E 2018, ' A novel adeno-associated virus capsid with enhanced neurotropism corrects a lysosomal transmembrane enzyme deficiency ', Brain, vol. 141, no. 7, pp. 2014-2031 . https://doi.org/10.1093/brain/awy126

مصطلحات موضوعية: 0301 basic medicine, Male, Neurotropism, Mucopolysaccharidosis, Genetic enhancement, viruses, medicine.disease_cause, Protein Engineering, Rats, Sprague-Dawley, Transduction (genetics), Mice, Mucopolysaccharidosis III, Transduction, Genetic, GENE-THERAPY VECTOR, Lysosomal storage disease, Tissue Distribution, Adeno-associated virus, VIRAL VECTORS, neurotropism, mucopolysaccharidosis, MOUSE MODEL, HEPARAN-SULFATE PROTEOGLYCAN, Dependovirus, 3. Good health, Cell biology, Capsid, CONGENITAL AMAUROSIS, Female, Life Sciences & Biomedicine, lysosomal transmembrane enzyme, RECEPTOR FOOTPRINT, Genetic Vectors, Clinical Neurology, adeno-associated virus, Biology, SANFILIPPO-SYNDROME, Virus, Retina, capsid engineering, 03 medical and health sciences, medicine, Animals, Photoreceptor Cells, HIPPOCAMPAL-LESIONS, Science & Technology, MUCOPOLYSACCHARIDOSIS-IIIB, Neurosciences, Original Articles, Genetic Therapy, NEURONAL CEROID-LIPOFUSCINOSIS, medicine.disease, Rats, Mice, Inbred C57BL, 030104 developmental biology, Neurosciences & Neurology, Neurology (clinical)

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URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::5b17a7608215d5ccd1f1e0191c5e9330