دورية أكاديمية

European Medicines Agency review of ataluren for the treatment of ambulant patients aged 5 years and older with Duchenne muscular dystrophy resulting from a nonsense mutation in the dystrophin gene

التفاصيل البيبلوغرافية
العنوان: European Medicines Agency review of ataluren for the treatment of ambulant patients aged 5 years and older with Duchenne muscular dystrophy resulting from a nonsense mutation in the dystrophin gene
المؤلفون: Haas, Manuel *, Vlcek, Viktor, Balabanov, Pavel, Salmonson, Tomas, Bakchine, Serge, Markey, Greg, Weise, Martina, Schlosser-Weber, Gabriele, Brohmann, Henning, Yerro, Concepcion Prieto, Mendizabal, Macarena Rodriguez, Stoyanova-Beninska, Violeta, Hillege, Hans L.
المصدر: In Neuromuscular Disorders January 2015 25(1):5-13
قاعدة البيانات: ScienceDirect
الوصف
تدمد:09608966
DOI:10.1016/j.nmd.2014.11.011