دورية أكاديمية

WHOLE-BODY GALACTOSE OXIDATION AS A ROBUST FUNCTIONAL ASSAY TO EVALUATE THE EFFECTIVENESS OF HGALT GENE-BASED THERAPIES IN A MOUSE MODEL OF CLASSIC GALACTOSEMIA

التفاصيل البيبلوغرافية
العنوان: WHOLE-BODY GALACTOSE OXIDATION AS A ROBUST FUNCTIONAL ASSAY TO EVALUATE THE EFFECTIVENESS OF HGALT GENE-BASED THERAPIES IN A MOUSE MODEL OF CLASSIC GALACTOSEMIA
المؤلفون: Balakrishnan, Bijina, Yan, Xinhua, Bellagamba, Olivia, Zimmer, Mike, Winkler, Felicity, McCue, Marshall, Martini, Paolo G.V., Lai, Kent
المصدر: In Molecular Genetics and Metabolism March 2023 138(3)
قاعدة البيانات: ScienceDirect
الوصف
تدمد:10967192
DOI:10.1016/j.ymgme.2023.107388