دورية أكاديمية
WHOLE-BODY GALACTOSE OXIDATION AS A ROBUST FUNCTIONAL ASSAY TO EVALUATE THE EFFECTIVENESS OF HGALT GENE-BASED THERAPIES IN A MOUSE MODEL OF CLASSIC GALACTOSEMIA
العنوان: | WHOLE-BODY GALACTOSE OXIDATION AS A ROBUST FUNCTIONAL ASSAY TO EVALUATE THE EFFECTIVENESS OF HGALT GENE-BASED THERAPIES IN A MOUSE MODEL OF CLASSIC GALACTOSEMIA |
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المؤلفون: | Balakrishnan, Bijina, Yan, Xinhua, Bellagamba, Olivia, Zimmer, Mike, Winkler, Felicity, McCue, Marshall, Martini, Paolo G.V., Lai, Kent |
المصدر: | In Molecular Genetics and Metabolism March 2023 138(3) |
قاعدة البيانات: | ScienceDirect |
تدمد: | 10967192 |
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DOI: | 10.1016/j.ymgme.2023.107388 |