دورية أكاديمية

Vestronidase alfa for the treatment of mucopolysaccharidosis type VII (MPS VII): Updated results from a novel, longitudinal, multi-center disease monitoring program (DMP)

التفاصيل البيبلوغرافية
العنوان: Vestronidase alfa for the treatment of mucopolysaccharidosis type VII (MPS VII): Updated results from a novel, longitudinal, multi-center disease monitoring program (DMP)
المؤلفون: Giugliani, Roberto, Grant, Christina L., Scarpa, Maurizio, Sun, Angela, Wang, Raymond Y., Burton, Barbara K., Oussoren, Esmeralda, Durand, Consuelo, Martins, Esmeralda E., Chabrol, Brigitte, Hetzer, Joel, Marsden, Deborah, Merritt, J. Lawrence, II, Gonzalez-Meneses, Antonio
المصدر: In Molecular Genetics and Metabolism February 2024 141(2)
قاعدة البيانات: ScienceDirect
الوصف
تدمد:10967192
DOI:10.1016/j.ymgme.2023.107851