دورية أكاديمية
Systemic gene therapy using an AAV44.9 vector rescues a neonatal lethal mouse model of propionic acidemia
العنوان: | Systemic gene therapy using an AAV44.9 vector rescues a neonatal lethal mouse model of propionic acidemia |
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المؤلفون: | Chandler, Randy J., Di Pasquale, Giovanni, Choi, Eun-Young, Chang, David, Smith, Stephanie N., Sloan, Jennifer L., Hoffmann, Victoria, Li, Lina, Chiorini, John A., Venditti, Charles P. |
المصدر: | In Molecular Therapy - Methods & Clinical Development 14 September 2023 30:181-190 |
قاعدة البيانات: | ScienceDirect |
تدمد: | 23290501 |
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DOI: | 10.1016/j.omtm.2023.06.008 |