دورية أكاديمية
Prevention of early-onset cardiomyopathy in Dmd exon 52–54 deletion mice by CRISPR-Cas9-mediated exon skipping
العنوان: | Prevention of early-onset cardiomyopathy in Dmd exon 52–54 deletion mice by CRISPR-Cas9-mediated exon skipping |
---|---|
المؤلفون: | Rok, Matthew, Wong, Tatianna Wai Ying, Maino, Eleonora, Ahmed, Abdalla, Yang, Grace, Hyatt, Elzbieta, Lindsay, Kyle, Fatehi, Sina, Marks, Ryan, Delgado-Olguín, Paul, Ivakine, Evgueni A., Cohn, Ronald D. |
المصدر: | In Molecular Therapy - Methods & Clinical Development 14 September 2023 30:246-258 |
قاعدة البيانات: | ScienceDirect |
تدمد: | 23290501 |
---|---|
DOI: | 10.1016/j.omtm.2023.07.004 |