دورية أكاديمية

Prevention of early-onset cardiomyopathy in Dmd exon 52–54 deletion mice by CRISPR-Cas9-mediated exon skipping

التفاصيل البيبلوغرافية
العنوان: Prevention of early-onset cardiomyopathy in Dmd exon 52–54 deletion mice by CRISPR-Cas9-mediated exon skipping
المؤلفون: Rok, Matthew, Wong, Tatianna Wai Ying, Maino, Eleonora, Ahmed, Abdalla, Yang, Grace, Hyatt, Elzbieta, Lindsay, Kyle, Fatehi, Sina, Marks, Ryan, Delgado-Olguín, Paul, Ivakine, Evgueni A., Cohn, Ronald D.
المصدر: In Molecular Therapy - Methods & Clinical Development 14 September 2023 30:246-258
قاعدة البيانات: ScienceDirect
الوصف
تدمد:23290501
DOI:10.1016/j.omtm.2023.07.004