التفاصيل البيبلوغرافية
العنوان: |
Whole-body galactose oxidation as a robust functional assay to assess the efficacy of gene-based therapies in a mouse model of Galactosemia |
المؤلفون: |
Balakrishnan, Bijina, Yan, Xinhua, McCue, Marshall D., Bellagamba, Olivia, Guo, Aaron, Winkler, Felicity, Thall, Jason, Crawford, Lisa, Dimen, Rain, Chen, Sara, McEnaney, Sean, Wu, Yiman, Zimmer, Mike, Sarkis, Joe, Martini, Paolo G.V., Finn, Patrick F., Lai, Kent |
المصدر: |
In Molecular Therapy - Methods & Clinical Development 14 March 2024 32(1) |
قاعدة البيانات: |
ScienceDirect |