التفاصيل البيبلوغرافية
العنوان: |
Investigating health-related quality of life in rare diseases: a case study in utility value determination for patients with CLN2 disease (neuronal ceroid lipofuscinosis type 2) |
المؤلفون: |
Gissen, PaulAff1, Specchio, Nicola, Olaye, Andrew, Jain, Mohit, Butt, Thomas, Ghosh, Wrik, Ruban-Fell, Benjamin, Griffiths, Annabel, Camp, Charlotte, Sisic, Zlatko, Schwering, Christoph, Wibbeler, Eva, Trivisano, Marina, Lee, Laura, Nickel, Miriam, Mortensen, Amanda, Schulz, Angela |
المصدر: |
Orphanet Journal of Rare Diseases. 16(1) |
قاعدة البيانات: |
Springer Nature Journals |