دورية أكاديمية

PB2314: OLIPUDASE ALFA FOR ADULTS WITH ACID SPHINGOMYELINASE DEFICIENCY: IMPROVEMENTS IN CROSSOVER PLACEBO PATIENTS AND FURTHER IMPROVEMENTS IN ORIGINAL OLIPUDASE ALFA PATIENTS AFTER 2 YEARS IN ASCEND TRIAL.

التفاصيل البيبلوغرافية
العنوان: PB2314: OLIPUDASE ALFA FOR ADULTS WITH ACID SPHINGOMYELINASE DEFICIENCY: IMPROVEMENTS IN CROSSOVER PLACEBO PATIENTS AND FURTHER IMPROVEMENTS IN ORIGINAL OLIPUDASE ALFA PATIENTS AFTER 2 YEARS IN ASCEND TRIAL.
المؤلفون: Villarrubia, J., Wasserstein, M., Barbato, A., Gallagher, R. C., Giugliani, R., Guelbert, N. B., Hennermann, J. B., Hollak, C., Ikezoe, T., Lachmann, R., Lidove, O., Mabe, P., Mengel, E., Scarpa, M., Senates, E., Tchan, M., Thurberg, B. L., Yarramaneni, A., Rawlings, A. M., Kim, Y.
المصدر: HemaSphere; 2022 Supplement 3, Vol. 6, p2183-2184, 2p
قاعدة البيانات: Complementary Index
الوصف
تدمد:25729241
DOI:10.1097/01.HS9.0000852080.43506.a5