دورية أكاديمية

Quantification of dystrophin to assess the effects of dystrophin-restoring treatments in Duchenne muscular dystrophy: Lessons from the development of eteplirsen.

التفاصيل البيبلوغرافية
العنوان: Quantification of dystrophin to assess the effects of dystrophin-restoring treatments in Duchenne muscular dystrophy: Lessons from the development of eteplirsen.
المؤلفون: Dworzak, Johannes, Frank, Diane E., Charleston, Jay S., Schnell, Frederick J., Voss, Jon, Donoghue, Cas, Milici, Anthony J., Aeffner, Famke, Young, G. David, Moore, Steven A., Lewis, Sarah, Peterson, Ellyn, Sahenk, Zarife, Shontz, Kimberly, Rodino-Klapac, Louise R., Mendell, Jerry R.
المصدر: European Journal of Paediatric Neurology; Jun2017 Supplement 1, Vol. 21, pe93-e94, 1p
قاعدة البيانات: Supplemental Index
الوصف
تدمد:10903798
DOI:10.1016/j.ejpn.2017.04.1209