Enhanced Version of Human Sulfamidase Significantly Ameliorates CNS Pathology When Delivered to the MPS-IIIA Mice by AAV-Mediated Intra-CSF Injection
العنوان: | Enhanced Version of Human Sulfamidase Significantly Ameliorates CNS Pathology When Delivered to the MPS-IIIA Mice by AAV-Mediated Intra-CSF Injection |
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المؤلفون: | Nicolina C. Sorrentino, Vincenzo Cacace, Veronica Maffia, Sandra Strollo, Novella Tedesco, Edoardo Nusco, Noemi Romagnoli, Domenico Ventrella, Francesca Barone, Maria laura Bacci, Yan Huang, Nan Liu, Susan Kalled, Vivian Choi, Alessandro Fraldi |
المساهمون: | Nicolina C. Sorrentino, Vincenzo Cacace, Veronica Maffia, Sandra Strollo, Novella Tedesco, Edoardo Nusco, Noemi Romagnoli, Domenico Ventrella, Francesca Barone, Maria laura Bacci, Yan Huang, Nan Liu, Susan Kalled, Vivian Choi, Alessandro Fraldi, Sorrentino, Nicolina C., Cacace, Vincenzo, Maffia, Veronica, Strollo, Sandra, Tedesco, Novella, Nusco, Edoardo, Romagnoli, Noemi, Ventrella, Domenico, Barone, Francesca, laura Bacci, Maria, Huang, Yan, Liu, Nan, Kalled, Susan, Choi, Vivian, Fraldi, Alessandro, Nicolina C. Sorrentino, Vincenzo Cacace, Veronica Maffia, Sandra Strollo, Novella Tedesco, Edoardo Nusco, Noemi Romagnoli, Domenico Ventrella, Francesca Barone, Maria laura Bacci, Yan Huang, Nan Liu, Susan Kalled, Vivian Choi, Alessandro Fraldi |
سنة النشر: | 2018 |
مصطلحات موضوعية: | Gene Therapy, MPS IIIA, Mice, Intra-CSF injection |
وصف الملف: | ELETTRONICO |
اللغة: | English |
URL الوصول: | https://explore.openaire.eu/search/publication?articleId=dedup_wf_001::b52b00c9a0fcffbf18aac2f0b0ee7b8e http://hdl.handle.net/11588/756658 |
حقوق: | CLOSED |
رقم الأكسشن: | edsair.dedup.wf.001..b52b00c9a0fcffbf18aac2f0b0ee7b8e |
قاعدة البيانات: | OpenAIRE |
الوصف غير متاح. |