Enhanced Version of Human Sulfamidase Significantly Ameliorates CNS Pathology When Delivered to the MPS-IIIA Mice by AAV-Mediated Intra-CSF Injection

التفاصيل البيبلوغرافية
العنوان: Enhanced Version of Human Sulfamidase Significantly Ameliorates CNS Pathology When Delivered to the MPS-IIIA Mice by AAV-Mediated Intra-CSF Injection
المؤلفون: Nicolina C. Sorrentino, Vincenzo Cacace, Veronica Maffia, Sandra Strollo, Novella Tedesco, Edoardo Nusco, Noemi Romagnoli, Domenico Ventrella, Francesca Barone, Maria laura Bacci, Yan Huang, Nan Liu, Susan Kalled, Vivian Choi, Alessandro Fraldi
المساهمون: Nicolina C. Sorrentino, Vincenzo Cacace, Veronica Maffia, Sandra Strollo, Novella Tedesco, Edoardo Nusco, Noemi Romagnoli, Domenico Ventrella, Francesca Barone, Maria laura Bacci, Yan Huang, Nan Liu, Susan Kalled, Vivian Choi, Alessandro Fraldi, Sorrentino, Nicolina C., Cacace, Vincenzo, Maffia, Veronica, Strollo, Sandra, Tedesco, Novella, Nusco, Edoardo, Romagnoli, Noemi, Ventrella, Domenico, Barone, Francesca, laura Bacci, Maria, Huang, Yan, Liu, Nan, Kalled, Susan, Choi, Vivian, Fraldi, Alessandro, Nicolina C. Sorrentino, Vincenzo Cacace, Veronica Maffia, Sandra Strollo, Novella Tedesco, Edoardo Nusco, Noemi Romagnoli, Domenico Ventrella, Francesca Barone, Maria laura Bacci, Yan Huang, Nan Liu, Susan Kalled, Vivian Choi, Alessandro Fraldi
سنة النشر: 2018
مصطلحات موضوعية: Gene Therapy, MPS IIIA, Mice, Intra-CSF injection
وصف الملف: ELETTRONICO
اللغة: English
URL الوصول: https://explore.openaire.eu/search/publication?articleId=dedup_wf_001::b52b00c9a0fcffbf18aac2f0b0ee7b8e
http://hdl.handle.net/11588/756658
حقوق: CLOSED
رقم الأكسشن: edsair.dedup.wf.001..b52b00c9a0fcffbf18aac2f0b0ee7b8e
قاعدة البيانات: OpenAIRE