التفاصيل البيبلوغرافية
| العنوان: |
Lentiviral haematopoietic stem cell gene therapy for metachromatic leukodystrophy: Results in 5 patients treated under nominal compassionate use |
| المؤلفون: |
Valeria Calbi, Francesca Fumagalli, Vera Gallo, Salvatore Recupero, Fabiola De Mattia, Elena Sophia Fratini, Ambra Corti, Giulia Tarantola, Marina Sarzana, Alessia Ippolito, Stefano Scarparo, Francesca Ciotti, Maddalena Fraschini, Margherita Levi, Mara Sangalli, Francesco Morena, Sabata Martino, Caroline Sevin, Vinodh Narayanan, Etai Adam, Lisa Emrick, Roberto Giugliani, Alessandro Aiuti |
| المصدر: |
Molecular Genetics and Metabolism. 138:107044 |
| بيانات النشر: |
Elsevier BV, 2023. |
| سنة النشر: |
2023 |
| مصطلحات موضوعية: |
Endocrinology, Endocrinology, Diabetes and Metabolism, Genetics, Molecular Biology, Biochemistry |
| تدمد: |
1096-7192 |
| URL الوصول: |
https://explore.openaire.eu/search/publication?articleId=doi_________::2a354d438c53ad77b6c584626d9c478a
https://doi.org/10.1016/j.ymgme.2022.107044 |
| حقوق: |
CLOSED |
| رقم الأكسشن: |
edsair.doi...........2a354d438c53ad77b6c584626d9c478a |
| قاعدة البيانات: |
OpenAIRE |
