Long‐term safety and efficacy of velmanase alfa treatment in children under 6 years of age with alpha‐mannosidosis: A phase 2, open label, multicenter study
| العنوان: | Long‐term safety and efficacy of velmanase alfa treatment in children under 6 years of age with alpha‐mannosidosis: A phase 2, open label, multicenter study |
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| المؤلفون: | Nathalie Guffon, Vassiliki Konstantopoulou, Julia B. Hennermann, Nicole Muschol, Irene Bruno, Albina Tummolo, Ferdinando Ceravolo, Giulia Zardi, Andrea Ballabeni, Allan Lund |
| المصدر: | Journal of Inherited Metabolic Disease. |
| بيانات النشر: | Wiley, 2023. |
| سنة النشر: | 2023 |
| مصطلحات موضوعية: | Genetics, Genetics (clinical) |
| تدمد: | 1573-2665 0141-8955 |
| URL الوصول: | https://explore.openaire.eu/search/publication?articleId=doi_________::3b94d1a892d9eef487248743099cb425 https://doi.org/10.1002/jimd.12602 |
| حقوق: | OPEN |
| رقم الأكسشن: | edsair.doi...........3b94d1a892d9eef487248743099cb425 |
| قاعدة البيانات: | OpenAIRE |
| تدمد: | 15732665 01418955 |
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