دورية أكاديمية
Enzyme replacement therapy with a blood brain barrier-penetrating antibody-fused alpha-L-iduronidase prevents bone deformities in a mouse model of mucopolysaccharidosis type I
العنوان: | Enzyme replacement therapy with a blood brain barrier-penetrating antibody-fused alpha-L-iduronidase prevents bone deformities in a mouse model of mucopolysaccharidosis type I |
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المؤلفون: | Morioka, Hiroki, Morimoto, Hideto, Aoki, Nao, Ito, Jun, Hirato, Toru, Sonoda, Hiroyuki, Minami, Kohtaro |
المصدر: | In Molecular Genetics and Metabolism February 2024 141(2) |
قاعدة البيانات: | ScienceDirect |
تدمد: | 10967192 |
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DOI: | 10.1016/j.ymgme.2023.107968 |