التفاصيل البيبلوغرافية
العنوان: |
Olipudase alfa enzyme replacement therapy reverses interstitial lung disease in adults with acid sphingomyelinase deficiency: Long-term pulmonary outcomes of the ASCEND trial |
المؤلفون: |
Wasserstein, Melissa, Bonella, Francesco, Giugliani, Roberto, Lachmann, Robin, Noth, Imre, Scarpa, Maurizio, Wuyts, Wim A., Aguiar, Mario, Armstrong, Nicole, Kumar, Monica, Berger, Kenneth |
المصدر: |
In Molecular Genetics and Metabolism February 2024 141(2) |
قاعدة البيانات: |
ScienceDirect |