دورية أكاديمية

Olipudase alfa enzyme replacement therapy reverses interstitial lung disease in adults with acid sphingomyelinase deficiency: Long-term pulmonary outcomes of the ASCEND trial

التفاصيل البيبلوغرافية
العنوان: Olipudase alfa enzyme replacement therapy reverses interstitial lung disease in adults with acid sphingomyelinase deficiency: Long-term pulmonary outcomes of the ASCEND trial
المؤلفون: Wasserstein, Melissa, Bonella, Francesco, Giugliani, Roberto, Lachmann, Robin, Noth, Imre, Scarpa, Maurizio, Wuyts, Wim A., Aguiar, Mario, Armstrong, Nicole, Kumar, Monica, Berger, Kenneth
المصدر: In Molecular Genetics and Metabolism February 2024 141(2)
قاعدة البيانات: ScienceDirect
الوصف
تدمد:10967192
DOI:10.1016/j.ymgme.2023.108075