دورية أكاديمية

Combination HSCT and intravenous AAV-mediated gene therapy in a canine model proves pivotal for translation of Krabbe disease therapy

التفاصيل البيبلوغرافية
العنوان: Combination HSCT and intravenous AAV-mediated gene therapy in a canine model proves pivotal for translation of Krabbe disease therapy
المؤلفون: Bradbury, Allison M., Bagel, Jessica, Swain, Gary, Miyadera, Keiko, Pesayco, Jill P., Assenmacher, Charles-Antoine, Brisson, Becky, Hendricks, Ian, Wang, Xiao H., Herbst, Zachary, Pyne, Nettie, Odonnell, Patricia, Shelton, G. Diane, Gelb, Michael, Hackett, Neil, Szabolcs, Paul, Vite, Charles H., Escolar, Maria
المصدر: In Molecular Therapy 3 January 2024 32(1):44-58
قاعدة البيانات: ScienceDirect
الوصف
تدمد:15250016
DOI:10.1016/j.ymthe.2023.11.014