دورية أكاديمية

Hematopoietic stem cell gene therapy improves outcomes in a clinically relevant mouse model of multiple sulfatase deficiency

التفاصيل البيبلوغرافية
العنوان: Hematopoietic stem cell gene therapy improves outcomes in a clinically relevant mouse model of multiple sulfatase deficiency
المؤلفون: Pham, Vi, Tricoli, Lucas, Hong, Xinying, Wongkittichote, Parith, Castruccio Castracani, Carlo, Guerra, Amaliris, Schlotawa, Lars, Adang, Laura A., Kuhs, Amanda, Cassidy, Margaret M., Kane, Owen, Tsai, Emily, Presa, Maximiliano, Lutz, Cathleen, Rivella, Stefano B., Ahrens-Nicklas, Rebecca C.
المصدر: In Molecular Therapy August 2024
قاعدة البيانات: ScienceDirect
الوصف
تدمد:15250016
DOI:10.1016/j.ymthe.2024.08.015