دورية أكاديمية
DNA base editing corrects common hemophilia A mutations and restores factor VIII expression in in vitro and ex vivo models
| العنوان: | DNA base editing corrects common hemophilia A mutations and restores factor VIII expression in in vitro and ex vivo models |
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| المؤلفون: | Tonetto, Elena, Cucci, Alessia, Follenzi, Antonia, Bernardi, Francesco, Pinotti, Mirko, Balestra, Dario |
| المصدر: | In Journal of Thrombosis and Haemostasis August 2024 22(8):2171-2183 |
| قاعدة البيانات: | ScienceDirect |
| تدمد: | 15387836 |
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| DOI: | 10.1016/j.jtha.2024.04.020 |