دورية أكاديمية

Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTT

التفاصيل البيبلوغرافية
العنوان: Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTT
المؤلفون: Iwamoto, Naoki, Liu, Yuanjing, Frank-Kamenetsky, Maria, Maguire, Abbie, Tseng, Wei Chou, Taborn, Kristin, Kothari, Nayantara, Akhtar, Ali, Bowman, Keith, Shelke, Juili Dilip, Lamattina, Anthony, Hu, Xiao Shelley, Jang, Hyun Gyung, Kandasamy, Pachamuthu, Liu, Fangjun, Longo, Ken, Looby, Richard, Meena, Metterville, Jake, Pan, Qianli, Purcell-Estabrook, Erin, Shimizu, Mamoru, Prakasha, Priyanka Shiva, Standley, Stephany, Upadhyay, Hansini, Yang, Hailin, Yin, Yuan, Zhao, Anderson, Francis, Christopher, Byrne, Mike, Dale, Elena, Verdine, Gregory L., Vargeese, Chandra
المصدر: In Molecular Therapy - Nucleic Acids 10 September 2024 35(3)
قاعدة البيانات: ScienceDirect
الوصف
تدمد:21622531
DOI:10.1016/j.omtn.2024.102246