دورية أكاديمية

Whole-body galactose oxidation as a robust functional assay to assess the efficacy of gene-based therapies in a mouse model of Galactosemia

التفاصيل البيبلوغرافية
العنوان: Whole-body galactose oxidation as a robust functional assay to assess the efficacy of gene-based therapies in a mouse model of Galactosemia
المؤلفون: Balakrishnan, Bijina, Yan, Xinhua, McCue, Marshall D., Bellagamba, Olivia, Guo, Aaron, Winkler, Felicity, Thall, Jason, Crawford, Lisa, Dimen, Rain, Chen, Sara, McEnaney, Sean, Wu, Yiman, Zimmer, Mike, Sarkis, Joe, Martini, Paolo G.V., Finn, Patrick F., Lai, Kent
المصدر: In Molecular Therapy - Methods & Clinical Development 14 March 2024 32(1)
قاعدة البيانات: ScienceDirect
الوصف
تدمد:23290501
DOI:10.1016/j.omtm.2024.101191