دورية أكاديمية
A blood-brain barrier-penetrant AAV gene therapy improves neurological function in symptomatic mucolipidosis IV mice
| العنوان: | A blood-brain barrier-penetrant AAV gene therapy improves neurological function in symptomatic mucolipidosis IV mice |
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| المؤلفون: | Sangster, Madison L., Bishop, Martha M., Yao, Yizheng, Feitor, Jessica F., Shahriar, Sanjid, Miller, Maxwell E., Chekuri, Anil K., Budnik, Bogdan, Bei, Fengfeng, Grishchuk, Yulia |
| المصدر: | In Molecular Therapy - Methods & Clinical Development 13 June 2024 32(2) |
| قاعدة البيانات: | ScienceDirect |
Full Text Finder | تدمد: | 23290501 |
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| DOI: | 10.1016/j.omtm.2024.101269 |