دورية أكاديمية

Correction of β-thalassemia by CRISPR/Cas9 editing of the α-globin locus in human hematopoietic stem cells

التفاصيل البيبلوغرافية
العنوان: Correction of β-thalassemia by CRISPR/Cas9 editing of the α-globin locus in human hematopoietic stem cells
المؤلفون: Pavani, Giulia, Fabiano, Anna *, Laurent, Marine *, Amor, Fatima, Cantelli, Erika, Chalumeau, Anne, Maule, Giulia, Tachtsidi, Alexandra, Concordet, Jean-Paul, Cereseto, Anna, Mavilio, Fulvio, Ferrari, Giuliana, Miccio, Annarita, Amendola, Mario
المصدر: In Blood Advances 9 March 2021 5(5):1137-1153
قاعدة البيانات: ScienceDirect
الوصف
تدمد:24739529
DOI:10.1182/bloodadvances.2020001996