دورية أكاديمية

P261: Vestronidase alfa for the treatment of mucopolysaccharidosis VII (MPS VII): Updated results from a longitudinal, multicenter disease monitoring program (DMP)

التفاصيل البيبلوغرافية
العنوان: P261: Vestronidase alfa for the treatment of mucopolysaccharidosis VII (MPS VII): Updated results from a longitudinal, multicenter disease monitoring program (DMP)
المؤلفون: Giugliani, Roberto, Gonzalez-Meneses, Antonio, Grant, Christina, Scarpa, Maurizio, Sun, Angela, Wang, Raymond, Burton, Barbara, van der Ploeg, Ans, Martins, Esmeralda, Durand, Consuelo, Chabrol, Brigitte, Hetzer, Joel, Marsden, Deborah, Merritt, J. Lawrence, II
المصدر: In Genetics in Medicine Open 2024 2 Supplement 1
قاعدة البيانات: ScienceDirect
الوصف
تدمد:29497744
DOI:10.1016/j.gimo.2024.101157