دورية أكاديمية
Exon skipping restores dystrophin expression, but fails to prevent disease progression in later stage dystrophic dko mice
العنوان: | Exon skipping restores dystrophin expression, but fails to prevent disease progression in later stage dystrophic dko mice |
---|---|
المؤلفون: | Wu, BAff1, IDgt201453_cor1, Cloer, C, Lu, P, Milazi, S, Shaban, M, Shah, S N, Marston-Poe, L, Moulton, H M, Lu, Q LAff1, IDgt201453_cor9 |
المصدر: | Gene Therapy. 21(9):785-793 |
قاعدة البيانات: | Springer Nature Journals |
تدمد: | 09697128 14765462 |
---|---|
DOI: | 10.1038/gt.2014.53 |