دورية أكاديمية

Evaluation of the efficacy of cystinosin supplementation through CTNS mRNA delivery in experimental models for cystinosis

التفاصيل البيبلوغرافية
العنوان: Evaluation of the efficacy of cystinosin supplementation through CTNS mRNA delivery in experimental models for cystinosis
المؤلفون: Bondue, Tjessa, Berlingerio, Sante Princiero, Siegerist, Florian, Sendino-Garví, Elena, Schindler, Maximilian, Baelde, Hans Jacobus, Cairoli, Sara, Goffredo, Bianca Maria, Arcolino, Fanny OliveiraAff1, Aff6, Dieker, Jürgen, Janssen, Manoe Jacoba, Endlich, Nicole, Brock, RolandAff8, Aff9, Gijsbers, RikAff10, Aff11, van den Heuvel, LambertusAff1, Aff12, Levtchenko, ElenaAff1, Aff13, IDs4159802347085w_cor16
المصدر: Scientific Reports. 13(1)
قاعدة البيانات: Springer Nature Journals
الوصف
تدمد:20452322
DOI:10.1038/s41598-023-47085-w