التفاصيل البيبلوغرافية
العنوان: |
Disease characteristics, effectiveness, and safety of vestronidase alfa for the treatment of patients with mucopolysaccharidosis VII in a novel, longitudinal, multicenter disease monitoring program |
المؤلفون: |
Giugliani, RobertoAff1, IDs1302302403176z_cor1, Gonzalez-Meneses, Antonio, Scarpa, Maurizio, Burton, Barbara, Wang, Raymond, Martins, Esmeralda, Oussoren, Esmeralda, Hennermann, Julia B., Chabrol, Brigitte, Grant, Christina L., Sun, Angela, Durand, Consuelo, Hetzer, Joel, Malkus, Betsy, Marsden, Deborah, Merritt II, J. Lawrence |
المصدر: |
Orphanet Journal of Rare Diseases. 19(1) |
قاعدة البيانات: |
Springer Nature Journals |