دورية أكاديمية
Systemic messenger RNA as an etiological treatment for acute intermittent porphyria
العنوان: | Systemic messenger RNA as an etiological treatment for acute intermittent porphyria |
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المؤلفون: | Jiang, Lei, Berraondo, PedroAff2, Aff3, Aff4, Jericó, DanielAff3, Aff5, Guey, Lin T., Sampedro, AnaAff3, Aff5, Frassetto, Andrea, Benenato, Kerry E., Burke, Kristine, Santamaría, EvaAff3, Aff5, Aff6, Alegre, ManuelAff7, Aff8, Pejenaute, Álvaro, Kalariya, Mayur, Butcher, William, Park, Ji-Sun, Zhu, Xuling, Sabnis, Staci, Kumarasinghe, E. Sathyajith, Salerno, Timothy, Kenney, Matthew, Lukacs, Christine M., Ávila, Matías A.Aff3, Aff5, Aff6, Martini, Paolo G. V.Aff1, Fontanellas, AntonioAff3, Aff5, Aff6 |
المصدر: | Nature Medicine. 24(12):1899-1909 |
قاعدة البيانات: | Springer Nature Journals |
تدمد: | 10788956 1546170X |
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DOI: | 10.1038/s41591-018-0199-z |