التفاصيل البيبلوغرافية
العنوان: |
Long-term efficacy and safety of sapropterin in patients who initiated sapropterin at < 4 years of age with phenylketonuria: results of the 3-year extension of the SPARK open-label, multicentre, randomised phase IIIb trial |
المؤلفون: |
Muntau, Ania C.Aff1, Burlina, Alberto, Eyskens, François, Freisinger, Peter, Leuzzi, Vincenzo, Sivri, Hatice Serap, Gramer, Gwendolyn, Pazdírková, Renata, Cleary, Maureen, Lotz-Havla, Amelia S., Lane, Paul, Alvarez, Ignacio, Rutsch, Frank |
المصدر: |
Orphanet Journal of Rare Diseases. 16(1) |
قاعدة البيانات: |
Springer Nature Journals |