دورية أكاديمية
Neonatal gene therapy achieves sustained disease rescue of maple syrup urine disease in mice
العنوان: | Neonatal gene therapy achieves sustained disease rescue of maple syrup urine disease in mice |
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المؤلفون: | Pontoizeau, ClémentAff1, Aff2, Aff3, IDs4146702230880w_cor1, Simon-Sola, Marcelo, Gaborit, Clovis, Nguyen, Vincent, Rotaru, Irina, Tual, Nolan, Colella, Pasqualina, Girard, MurielAff5, Aff6, Biferi, Maria-Grazia, Arnoux, Jean-Baptiste, Rötig, Agnès, Ottolenghi, ChrisAff1, Aff2, Aff3, de Lonlay, PascaleAff2, Aff6, Mingozzi, Federico, Cavazzana, MarinaAff3, Aff8, Schiff, ManuelAff2, Aff3, IDs4146702230880w_cor16 |
المصدر: | Nature Communications. 13(1) |
قاعدة البيانات: | Springer Nature Journals |
تدمد: | 20411723 |
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DOI: | 10.1038/s41467-022-30880-w |