دورية أكاديمية

Neonatal gene therapy achieves sustained disease rescue of maple syrup urine disease in mice

التفاصيل البيبلوغرافية
العنوان: Neonatal gene therapy achieves sustained disease rescue of maple syrup urine disease in mice
المؤلفون: Pontoizeau, ClémentAff1, Aff2, Aff3, IDs4146702230880w_cor1, Simon-Sola, Marcelo, Gaborit, Clovis, Nguyen, Vincent, Rotaru, Irina, Tual, Nolan, Colella, Pasqualina, Girard, MurielAff5, Aff6, Biferi, Maria-Grazia, Arnoux, Jean-Baptiste, Rötig, Agnès, Ottolenghi, ChrisAff1, Aff2, Aff3, de Lonlay, PascaleAff2, Aff6, Mingozzi, Federico, Cavazzana, MarinaAff3, Aff8, Schiff, ManuelAff2, Aff3, IDs4146702230880w_cor16
المصدر: Nature Communications. 13(1)
قاعدة البيانات: Springer Nature Journals